H. B.
- Vonhof,
- H.B.,
- Van Breukelen,
- M.R.,
- Postma,
- O.,
- ...
T cell suicide gene therapy to aid haematopoietic stem cell transplantation (2005)
Graft versus host disease (GVHD) is a T cell mediated phenomenon that arises following allogeneic haematopoietic stem cell transplantation, and may be particularly severe in the context of human...
- Titman,
- P.S.,
- Morton,
- L.,
- Skucek,
- E.,
- ...
Failure of SCID-X1 gene therapy in older patients (2005)
Gene therapy has been shown to be a highly effective treatment for infants with typical X-linked severe combined immunodeficiency (SCID-X1, gammac-deficiency). For patients in whom previous...
- Rao,
- K.,
- Amrolia,
- P.J.,
- Jones,
- A.,
- ...
The optimal approach to stem cell transplantation in children with immunodeficiency who lack a matched family donor is controversial. Unrelated donor stem cell transplantation gives equivalent...
Patients with X-linked lymphoproliferative syndrome (XLP) experience excessive T cell proliferation after primary Epstein-Barr virus (EBV) infection, due to mutations in the signalling lymphocyte...
Summary:X-linked lymphoproliferative disease (XLP) is a rare immunodeficiency caused by mutations in the signaling lymphocyte activating molecule-associated protein/SH2D1A gene and characterized by a...
Gene therapy for severe combined immunodeficiencies (2005)
Severe combined immune deficiencies (SCIDs) are a group of monogenic diseases resulting in profound disturbances of lymphocyte development and function. Affected individuals are prone to...
- Gaspar,
- H.B.,
- Bjorkegren,
- E.,
- Parsley,
- K.,
- ...
- Gaspar,
- H.B.,
- Bjorkegren,
- E.,
- Parsley,
- K.,
- ...
- Cohen,
- J.,
- Gandhi,
- M.,
- Naik,
- P.,
- ...
- Busby,
- M.,
- Gabrielsson,
- A.,
- Matousek,
- P.,
- ...
Successful gene therapy of SCID-X1 using a pseudotyped gammaretroviral vector (2004)
- Gaspar,
- H.B.,
- Parsley,
- K.,
- Howe,
- S.,
- ...
- Rao,
- K.,
- Amrolia,
- P.J.,
- Jones,
- A.,
- ...
The optimal approach to stem cell transplantation in children with immunodeficiency who lack a matched family donor is controversial. Unrelated donor stem cell transplant gives equivalent outcome to...
Nonmyeloablative stem cell transplantation for congenital immunodeficiencies (2000)
- Amrolia,
- P.,
- Gaspar,
- H.B.,
- Hassan,
- A.,
- ...
- McDade,
- H.B.,
- O'Hare,
- M.,
- Barry,
- M.,
- ...