Choesmel, Valérie, Fribourg, Sébastien, Aguissa-Touré, Almass-Houd, Pinaud, Noël, Legrand, Pierre, Gazda, Hanna T., ...
Diamond-Blackfan anemia (DBA) is a rare congenital disease affecting erythroid precursor differentiation. DBA is emerging as a paradigm for a new class of pathologies potentially linked to disorders...
Sanoudou, Despina, Haslett, Judith N., Kho, Alvin T., Guo, Shaoqiang, Gazda, Hanna T., Greenberg, Steven A., ...
The nemaline myopathies (NMs) are a clinically and genetically heterogeneous group of disorders characterized by nemaline rods and skeletal muscle weakness. Mutations in five sarcomeric thin filament...
Sanoudou, Despina, Haslett, Judith N., Kho, Alvin T., Guo, Shaoqiang, Gazda, Hanna T., Greenberg, Steven A., ...
The nemaline myopathies (NMs) are a clinically and genetically heterogeneous group of disorders characterized by nemaline rods and skeletal muscle weakness. Mutations in five sarcomeric thin filament...
Gazda, Hanna T., Sheen, Mee Rie, Vlachos, Adrianna, Choesmel, Valerie, O'Donohue, Marie-Françoise, Schneider, Hal, ...
Diamond-Blackfan anemia (DBA), a congenital bone-marrow-failure syndrome, is characterized by red blood cell aplasia, macrocytic anemia, clinical heterogeneity, and increased risk of malignancy....
Abnormalities of the large ribosomal subunit protein, Rpl35a, in Diamond-Blackfan anemia
Farrar, Jason E., Nater, Michelle, Caywood, Emi, McDevitt, Michael A., Kowalski, Jeanne, Takemoto, Clifford M., ...
Diamond-Blackfan anemia (DBA) is an inherited bone marrow failure syndrome characterized by anemia, congenital abnormalities, and cancer predisposition. Small ribosomal subunit genes RPS19, RPS24,...